In this episode, Dr. Paloma Giangrande, Editor-in-Chief of Molecular Therapy Nucleic Acids, speaks with Normand Allaire, Head of Genomics at the Cystic Fibrosis Foundation Therapeutics Lab. They discuss the article, Upregulation of a CFTR mRNA isoform has therapeutic potential for the treatment of 3’ CFTR PTC variants, which introduces an ASO-based therapeutic approach to cystic fibrosis for the 10% of patients who lack an approved treatment.

Music: 'Electric Dreams' by Scott Buckley - released under CC-BY 4.0. www.scottbuckley.com.au

In this episode, Dr. Paloma Giangrande, Editor-in-Chief of Molecular Therapy Nucleic Acids, speaks with Normand Allaire, Head of Genomics at the Cystic Fibrosis Foundation Therapeutics Lab. They discuss the article, Upregulation of a CFTR mRNA isoform has therapeutic potential for the treatment of 3&rsquo; CFTR PTC variants, which introduces an ASO-based therapeutic approach to cystic fibrosis for the 10% of patients who lack an approved treatment.
Music:&nbsp;'Electric Dreams' by Scott Buckley - released under CC-BY 4.0.&nbsp;<a href="https://www.scottbuckley.com.au/">www.scottbuckley.com.au</a>

The American Society of Gene & Cell Therapy is the premier membership organization for professionals working in cell and gene therapy. On this network, we're sharing exciting stories from our members and the greater scientific community.

The American Society of Gene &amp; Cell Therapy is the premier membership organization for professionals working in cell and gene therapy. On this network, we're sharing exciting stories from our members and the greater scientific community.

ASGCT Podcast Network

A CFTR mRNA isoform for the treatment of 3’ CFTR PTC variants with Normand Allaire

Recorded on site at the ASGCT 2026 Annual Meeting in Boston, this mini podcast series introduces listeners to ASGCT members and the work driving progress across the cell and gene therapy field. In each episode, members are invited to share their backgrounds, discuss the current state of the field, and reflect on the value of ASGCT membership. This series of brief, engaging conversations will help listeners get to know the people, perspectives, and ideas shaping the ASGCT community.

In this episode of Member Minutes, get to know Marco Carpenter, PhD, of the Children's Hospital of Philadelphia. Dr. Carpenter is one of the 2026 ASGCT Career Development Award recipients. Interviewed by Ben McLeod of the ASGCT Communications Committee, Dr. Carpenter also shares why ASGCT membership is valuable to his career.

Music: 'Origami' by Scott Buckley - released under CC-BY 4.0. www.scottbuckley.com.au

Recorded on site at the ASGCT 2026 Annual Meeting in Boston, this mini podcast series introduces listeners to ASGCT members and the work driving progress across the cell and gene therapy field. In each episode, members are invited to share their backgrounds, discuss the current state of the field, and reflect on the value of ASGCT membership. This series of brief, engaging conversations will help listeners get to know the people, perspectives, and ideas shaping the ASGCT community.
In this episode of Member Minutes, get to know Marco Carpenter, PhD, of the Children's Hospital of Philadelphia. Dr. Carpenter is one of the 2026 ASGCT Career Development Award recipients. Interviewed by Ben McLeod of the ASGCT Communications Committee, Dr. Carpenter also shares why ASGCT membership is valuable to his career.
Music: 'Origami' by Scott Buckley - released under CC-BY 4.0.&nbsp;<a href="https://url.us.m.mimecastprotect.com/s/IkczCERmXJSyRj4iNfxU7G5vB" data-auth="NotApplicable" data-linkindex="0">www.scottbuckley.com.au</a>

Member Minutes: Marco Carpenter, PhD

Recorded and published daily during #ASGCT2026, Soundbites of the Annual Meeting captures the energy and breadth of the conference through quick-hit conversations, scientific snapshots, attendee perspectives, and highlights from across the field — offering a daily pulse on what’s happening throughout the meeting.

Take a listen from Friday, May 15, 2026 as we talk with Jennifer Adair, PhD, the 2026 recipient of the Award for Excellence in Advancing Diversity, Equity, and Inclusion. She is joined by members of her lab, Motahareh Arjomandnejad, PhD, Rachel Cunningham, PhD, and two visiting scientists from Uganda who are part of an active NIH partnership with the lab to develop capacity for CGT for the treatment of HIV, Dr. George Ssenyange, MD and Gertrude N. Kiwanuka, PhD.

The group shares details of their work and their takeaways from the 2026 Annual Meeting.

 

This soundbite is hosted by Ben McLeod of the ASGCT Communications Committee.

Music: Everything Connected by High Street Music.

Recorded and published daily during #ASGCT2026, Soundbites of the Annual Meeting captures the energy and breadth of the conference through quick-hit conversations, scientific snapshots, attendee perspectives, and highlights from across the field &mdash; offering a daily pulse on what&rsquo;s happening throughout the meeting.
Take a listen from Friday, May 15, 2026 as we talk with Jennifer Adair, PhD, the 2026 recipient of the Award for Excellence in Advancing Diversity, Equity, and Inclusion. She is joined by members of her lab, Motahareh Arjomandnejad, PhD, Rachel Cunningham, PhD, and two visiting scientists from Uganda who are part of an active NIH partnership with the lab to develop capacity for CGT for the treatment of HIV, Dr. George Ssenyange, MD and Gertrude N. Kiwanuka, PhD.
The group shares details of their work and their takeaways from the 2026 Annual Meeting.
&nbsp;
This soundbite is hosted by Ben McLeod of the ASGCT Communications Committee.
Music: Everything Connected by High Street Music.

Soundbites Featuring Jennifer Adair, PhD; Motahareh Arjomandnejad, PhD; Rachel Cunningham, PhD; Dr. George Ssenyange, MD; and Gertrude N. Kiwanuka, PhD

Recorded and published daily during #ASGCT2026, Soundbites of the Annual Meeting captures the energy and breadth of the conference through quick-hit conversations, scientific snapshots, attendee perspectives, and highlights from across the field — offering a daily pulse on what’s happening throughout the meeting.

Take a listen from Friday, May 15, 2026 as we talk with Dr. Daria Fedyukina from ARPA-H, who was a panelist during the Fireside Chat, Engaging with ARPA-H—Funding priorities and future directions. The discussion centers around Dr. Fedyukina’s role at ARPA-H and some of the funded projects and companies she is working with.

This soundbite is hosted by Ben McLeod of the ASGCT Communications Committee.

Music: Everything Connected by High Street Music.

Recorded and published daily during #ASGCT2026, Soundbites of the Annual Meeting captures the energy and breadth of the conference through quick-hit conversations, scientific snapshots, attendee perspectives, and highlights from across the field &mdash; offering a daily pulse on what&rsquo;s happening throughout the meeting.
Take a listen from Friday, May 15, 2026 as we talk with Dr. Daria Fedyukina from ARPA-H, who was a panelist during the Fireside Chat, Engaging with ARPA-H&mdash;Funding priorities and future directions. The discussion centers around Dr. Fedyukina&rsquo;s role at ARPA-H and some of the funded projects and companies she is working with.
This soundbite is hosted by Ben McLeod of the ASGCT Communications Committee.
Music: Everything Connected by High Street Music.

A CFTR mRNA isoform for the treatment of 3’ CFTR PTC variants with Normand Allaire

In 1 playlist(s)

ASGCT Podcast Network

Social links

Follow podcast

Recent clips