Molecular Therapy Editor-in-Chief Dr. Joseph Glorioso joins researchers Kathy Steece-Collier (Michigan State University), Jeffrey Kordower (Arizona State University), and Fredric Manfredsson (Barrow Neurological Institute) to discuss their groundbreaking work on RNA interference for Parkinson’s disease. This episode focuses on their recent article titled "Disease-modifying, multidimensional efficacy of putaminal CaV1.3-shRNA gene therapy in aged parkinsonism male and female macaques."

Music: 'Electric Dreams' by Scott Buckley - released under CC-BY 4.0. www.scottbuckley.com.au

Molecular Therapy Editor-in-Chief Dr. Joseph Glorioso joins researchers Kathy Steece-Collier (Michigan State University), Jeffrey Kordower (Arizona State University), and Fredric Manfredsson (Barrow Neurological Institute) to discuss their groundbreaking work on RNA interference for Parkinson&rsquo;s disease. This episode focuses on their recent article titled "Disease-modifying, multidimensional efficacy of putaminal CaV1.3-shRNA gene therapy in aged parkinsonism male and female macaques."
Music:&nbsp;'Electric Dreams' by Scott Buckley - released under CC-BY 4.0.&nbsp;<a href="https://www.scottbuckley.com.au/">www.scottbuckley.com.au</a>

The American Society of Gene & Cell Therapy is the premier membership organization for professionals working in cell and gene therapy. On this network, we're sharing exciting stories from our members and the greater scientific community.

The American Society of Gene &amp; Cell Therapy is the premier membership organization for professionals working in cell and gene therapy. On this network, we're sharing exciting stories from our members and the greater scientific community.

ASGCT Podcast Network

RNA interference gene therapy for Parkinson’s disease with Kathy Steece-Collier, Jeffrey Kordower, and Fredric Manfredsson

Join host Emily Walsh Martin, PhD, as she hands the baton to the new co-hosts of The Issue podcast, Sanjay D’Souza, PhD, and Jason West, PhD. Listen in as the three preview some of the abstracts that will be presented at the ASGCT 2026 Annual Meeting, held May 11-15 in Boston, MA.

Music: ‘Bright New Morning’ by Steven O’Brien – released under CC-BY 4.0. https://www.steven-obrien.net/

Join host Emily Walsh Martin, PhD, as she hands the baton to the new co-hosts of The Issue podcast, Sanjay D&rsquo;Souza, PhD, and Jason West, PhD. Listen in as the three preview some of the abstracts that will be presented at the ASGCT 2026 Annual Meeting, held May 11-15 in Boston, MA.
Music:&nbsp;&lsquo;Bright New Morning&rsquo; by Steven O&rsquo;Brien &ndash; released under CC-BY 4.0.&nbsp;<a href="https://www.steven-obrien.net/">https://www.steven-obrien.net/</a>

ASGCT 2026 Abstract Highlights with Emily Walsh Martin, Sanjay D’Souza, and Jason West

In this episode, host Emily Walsh Martin revisits her 2022 Caregiver’s Perspective interview with Amber Freed, founder of SLC6A1 Connect. Amber is a caregiver to her son Maxwell, who has since received treatment for SLC6A1. Emily and Amber discuss Maxwell’s treatment and the role a caregiver plays in that journey.

Music: ‘Bright New Morning’ by Steven O’Brien – released under CC-BY 4.0. https://www.steven-obrien.net/

In this episode, host Emily Walsh Martin revisits her&nbsp;<a href="https://omny.fm/shows/asgct-podcast-network/key-considerations-of-gene-therapy-development-a-caregivers-story" data-auth="NotApplicable" data-linkindex="1">2022 Caregiver&rsquo;s Perspective interview with Amber Freed</a>, founder of SLC6A1 Connect. Amber is a caregiver to her son Maxwell, who has since received treatment for SLC6A1. Emily and Amber discuss Maxwell&rsquo;s treatment and the role a caregiver plays in that journey.
Music:&nbsp;&lsquo;Bright New Morning&rsquo; by Steven O&rsquo;Brien &ndash; released under CC-BY 4.0.&nbsp;<a href="https://www.steven-obrien.net/">https://www.steven-obrien.net/</a>

The Issue – A Caregiver’s Journey from Development to Treatment with Amber Freed, Founder of SLC6A1 Connect

In this episode, Molecular Therapy Editor-in-Chief Dr. Joseph Glorioso and Dr. Rita Perlingeiro (University of Minnesota) will discuss an article recently published in Molecular Therapy titled, “Preclinical quality, safety, and efficacy of a CGMP iPSC-derived myogenic progenitor product for the treatment of muscular dystrophies.”

Music: 'Electric Dreams' by Scott Buckley - released under CC-BY 4.0. www.scottbuckley.com.au

In this episode,&nbsp;Molecular Therapy&nbsp;Editor-in-Chief Dr. Joseph Glorioso and Dr. Rita Perlingeiro (University of Minnesota) will discuss an article recently published in&nbsp;Molecular Therapy&nbsp;titled, &ldquo;<a href="https://www.cell.com/molecular-therapy-family/molecular-therapy/fulltext/S1525-0016(25)00543-X">Preclinical quality, safety, and efficacy of a CGMP iPSC-derived myogenic progenitor product for the treatment of muscular dystrophies</a>.&rdquo;
Music:&nbsp;'Electric Dreams' by Scott Buckley - released under CC-BY 4.0.&nbsp;<a href="https://www.scottbuckley.com.au/">www.scottbuckley.com.au</a>

RNA interference gene therapy for Parkinson’s disease with Kathy Steece-Collier, Jeffrey Kordower, and Fredric Manfredsson

ASGCT Podcast Network

In 1 playlist(s)

ASGCT Podcast Network

Social links

Follow podcast

Recent clips